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See AllArticle In the Press The Journal of Pharmacology and Experimental Therapeutics: Tralesinidase Alfa Enzyme Replacement Therapy Prevents Disease Manifestations in a Canine Model of Mucopolysaccharidosis
Article In the Press The Journal of Pediatrics: Longitudinal Natural History of Pediatric Subjects Affected with Mucopolysaccharidosis IIIB
A mother is desperately seeking access to a trial drug for her nine-year-old son that she hopes could save his life. Severine Hamilton is trying to obtain a prototype enzyme replacement therapy for he

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